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CRISPR prevents hearing loss in mice
Researchers use CRISPR-Cas9 to target a mutation in the Tmc1 gene that causes the loss of hair cells in the inner ear.
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Gene Therapy
Gene Therapy is the introduction of normal genes into cells in place of missing or defective ones in order to correct genetic disorders.
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Groundbreaking gene therapy trial set to cure haemophilia
A cure for haemophilia is one step closer, following results of a gene therapy trial led by the NHS in London.
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Charles River adds ERS License to CRISPR/Cas9 service offering
Charles River Laboratories International, Inc. announced the expansion of its CRISPR/Cas9 service offering with the addition of a license from ERS Genomics Limited.
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Exclusive speaker interview with Professor Nagy Habib – MiNA Therapeutics/Imperial College London
SMi are delighted to have, Nagy Habib, Head of HPB Surgery, Imperial College London and Co-Founder, MiNA Therapeutics, as the Keynote Address for day 1 at RNA Therapeutics 2018!
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Gene therapy may lower risk for heart disease
Researchers have tested whether a single injection of the gene, LeXis could slow down the development of heart disease...
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£2m collaboration to focus on gene and cell therapy
A leading gene and cell therapy group has announced a collaboration focusing on gene and cell therapy manufacturing..
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From cancer evolution to personalised therapies
A research team have studied how alterations in a tumour depend on each other and how these dependencies determine cancer evolution...
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Biological bypass shows promise in coronary artery disease
A new gene therapy that targets the heart and requires only one treatment session has been found safe for patients with coronary artery disease...
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CRISPR identifies essential genes for cancer immunotherapy
Researchers have used CRISPR to stop the expression of individual genes in cancer cells, by knocking out every known protein-encoding gene in the human genome...
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CRISPR-Cas9 repairs genetic mutation in human embryos
"Well thought through and brilliantly executed" study shows different DNA-repair mechanism in embryos compared to iPSCs
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Researchers find new genes link to arthritis in bone marrow lesions
Researchers have found a pattern of genes which is characteristic of osteoarthritis and may be a step towards better treatments for this condition.
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Largest genome-wide study of lung cancer susceptibility conducted
A new study conducted by an international team of lung cancer researchers have identified new genetic variants for lung cancer risk.
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Ryboquin raises £1.8m for drug development in gene therapy
This latest funding round attracts two prominent new investors; Brian Kennedy and Sir Brian Souter.
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Dynamic DNA helps ward off gene damage
MRC-funded researchers have identified properties in DNA’s protective structure that could transform the way scientists think about the human genome.
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Queen’s researchers breakthrough discovery in fight against bowel cancer
New research led by Queen’s University Belfast has discovered how a genomic approach to understanding bowel cancer could improve the prognosis and quality of life for patients.