Potential treatment for neurological disorders targets brain cells
UCL researchers have developed a possible new treatment for neurological and psychiatric diseases, that works by reducing the excitability of overactive brain cells.
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Gene Therapy is the introduction of normal genes into cells in place of missing or defective ones in order to correct genetic disorders.
UCL researchers have developed a possible new treatment for neurological and psychiatric diseases, that works by reducing the excitability of overactive brain cells.
MIT researchers have developed a technique that could help the production of monoclonal antibodies and other useful proteins.
Decibel Therapeutics has submitted an IND application for a Phase I/II trial of DB-OTO, a gene therapy candidate to restore hearing.
12 October 2022 | By Unchained Labs
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A newly developed AAV has shown promise at delivering gene therapies to the brain in mice and non-human primates.
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The researchers found that augmenting NPHP5 gene rescues cilia defects in light-sensing cells derived from ciliopathy patients.
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In rodent models of ALS, the introduced neuroprotective protein slowed disease progression and increased life span.
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Researchers have found that new sickle cell disease gene therapies depend on choosing the right laboratory mice.
Researchers have found that inherited mutations in the MINAR2 gene causes deafness. The findings suggest that deafness could be treated with genetic therapies.
Scientists have developed a new gene editor which uses a modified pair of molecular scissors that make nicks on opposite strands of the DNA at two different points.
Scientists have developed a technology that can improve targeting specific organs and tissue types in gene therapy.